We have an international reputation for undertaking pioneering clinical rare disease research. We work with many stakeholders, including charities, businesses, health organizations, and other universities, in the delivery of effective innovative and research-based solutions.
These partnerships help us accelerate positive change for families, patients, carers, researchers, health care professionals, the local health departments and member charities.
We are particularly grateful to those charities, agencies and organizations who help fund our work. We thank you.